Rare diseases are those that affect only a small percentage of the world’s population. Most rare diseases are genetic. We provide many gene-engineered mouse models which are helpful for new therapies exploration and orphan drug development.
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系統名:C57BL/6Smoc-C9orf72em1Smoc
維持形態:Sperm cryopreservation | SMOC番号:NM-KO-201246
病気の予測:autoimmune disease
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系統名:C57BL/6Smoc-Cftrem1Smoc
維持形態:Sperm cryopreservation | SMOC番号:NM-KO-210282
病気の予測:cystic fibrosis
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系統名:C57BL/6Smoc-Cldn16em1Smoc
維持形態:Embryo cryopreservation | SMOC番号:NM-KO-200632
病気の予測:renal hypomagnesemia 3
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系統名:C57BL/6Smoc-Col4a5em1(R471X)Smoc
維持形態:Repository Live | SMOC番号:NM-KI-200183
病気の予測:X-linked Alport syndrome
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系統名:C57BL/6Smoc-Cpoxem1Smoc
維持形態:Embryo cryopreservation | SMOC番号:NM-KO-200828
病気の予測:hereditary coproporphyria
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系統名:C57BL/6Smoc-Csf2em2Smoc
維持形態:Sperm cryopreservation | SMOC番号:NM-KO-190532
病気の予測:systemic lupus erythematosus, pulmonary alveolar proteinosis
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系統名:C57BL/6Smoc-Csf2rbem1Smoc
維持形態:Sperm cryopreservation | SMOC番号:NM-KO-190787
病気の予測:pulmonary alveolar proteinosis
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系統名:C57BL/6Smoc-Cyp4v3em1Smoc
維持形態:Repository Live | SMOC番号:NM-KO-200711
病気の予測:Bietti crystalline corneoretinal dystrophy
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